Opinion|Videos|August 28, 2024

Examining Trial Data on Omaveloxolone Efficacy

A physician examines clinical trial results that impact their approach to treating patients with Friedreich ataxia.

Episodes in this series
  • In 2023, a propensity matched comparison of MOXIe extension patients to an untreated cohort found a significant slowing of disease progression per mFARS of 3.0 points compared to 6.6 points, respectively. Are these results clinically meaningful for patients and how does this relate to your everyday clinical practice?

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