Barry Byrne, MD, PhD, pediatric cardiologist, director, Powell Gene Therapy Center, joined the University of Florida in 1997. Having taken on educational, clinical, and research roles alike, he is currently leading research efforts in the realm of rare diseases, particularly inherited muscular diseases.
Shaping Gene Therapy Approaches in Neuromuscular Disease
Adeno-associated virus (AAV)–mediated gene therapy was one of the focal points of this year's Muscular Dystrophy Association conference. Here, Barry Byrne, MD, PhD, University of Florida, speaks to the novel development of AAV gene therapy and its mechanism of action.